Secondary hemophagocytic lymphohistiocytosis following Zolgensma therapy: An evolving story on the innate response to systemic gene therapy
Mol Ther
.
2022 Dec 7;30(12):3503-3504.
doi: 10.1016/j.ymthe.2022.11.007.
Epub 2022 Nov 26.
Authors
Barry J Byrne
1
,
Melissa Elder
2
,
Carmen Leon-Astudillo
2
,
Manuela Corti
2
Affiliations
1
University of Florida, Department of Pediatrics, Gainesville, FL, USA. Electronic address: barry.byrne@ufl.edu.
2
University of Florida, Department of Pediatrics, Gainesville, FL, USA.
PMID:
36436512
PMCID:
PMC9734075
DOI:
10.1016/j.ymthe.2022.11.007
No abstract available
Publication types
Editorial
MeSH terms
Genetic Therapy* / adverse effects